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Mucopolysaccharidosis Market Dynamics and Advancements in Rare Disease CareMucopolysaccharidosis Market and the Growing Need for Specialized Therapies Mucopolysaccharidosis (MPS) is a group of rare inherited lysosomal storage disorders caused by the deficiency of enzymes required to break down glycosaminoglycans within the body. As these substances accumulate in tissues and organs, patients often experience severe complications involving the bones, joints,...0 Commentarii 0 Distribuiri 3K Views 0 previzualizare